Rare Disease Research

Copy RSS feed URL

What is an Orphan Drug?
Featured Post

Orphan Drugs: Developing Treatments for Rare Diseases

According to the FDA, millions of Americans are currently affected by more than 7,000 rare diseases, many of which do not have treatment options or are...

Aaron Carroll • Date: 2/28/18

Linda Mozzone

XLH patient says new drug is giving her hope for the future

At 55 years old, Linda Mozzone says she’s getting a second chance at life,...

Christina Griffiths • 9/10/18

If not me, then who?

If not me, then who?This simple yet powerful adage is what fuels the research...

Sara Buckallew • 2/28/18

What is an Orphan Drug?

Orphan Drugs: Developing Treatments for Rare Diseases

According to the FDA, millions of Americans are currently affected by more than 7,000...

Aaron Carroll • 2/28/18

Dr. Christopher James on the Huntington’s Disease Center of Excellence

By: Dr. Christopher JamesIndiana University School of Medicine is making strides in a variety...

Em Collins • 2/28/18

A Breath of Fresh Air for Research

At 7 years old, Stephanie Davis knew exactly what she wanted to be...

Emily McKnight • 2/27/18

Rare Disease: How Common is the Uncommon?

What defines a rare disease? In the United States, a rare disease is defined as...

Emily McKnight • 2/27/18